Gene Therapy

Definition of Gene Therapy as it relates to Science, Genetics, Mutation

Gene therapy involves the use of genetic material to repair, replace, or regulate defective genes, aiming to prevent or treat diseases caused by mutations. It represents a powerful tool for modifying gene expression in cells and tissues, with direct implications for genetics research and clinical applications underpinned by scientific discoveries. By targeting specific mutations, this therapeutic approach can alleviate the impact of genetic disorders, providing an innovative strategy within the realm of mutation studies and contributing to advancements in science, genetics, and healthcare.

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External Links

Expertise in Gene Therapy Vectors Development, AAV, Lentivirus, Adenovirus viral vectors Production and Recombinant Protein manufacturing | Genemedi
(Gene Therapy Vector Production Service) | Genemedi
Genehome | Gene Therapy Education
Industry-Leading Gene Cell Therapy CDMO CBM
Encoded Therapeutics – Translating Next-Generation Science into Transformative Gene Therapies
Yposkesi | European CDMO in gene therapy viral vector manufacturing-Yposkesi
Home - International Society for Cell & Gene Therapy
uniQure | A Global Leader in Gene Therapy
bluebird bio | Setting the standard for gene therapy
NMDP BioTherapies | Advancing Your Cell or Gene Therapy
Gnthon - Advancing gene therapy treatments for rare diseases